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PTC Therapeutics, Inc.Italfarmaco SpAReveraGen BioPharma, Inc.Solid Biosciences, Inc.Mitochon Pharmaceuticals, Inc.Epirium Bio, Inc.Duchenne UKSynthena AGSummit Therapeutics Ltd.Tarix Orphan LLC
F. Hoffmann-La Roche Ltd.Takeda Pharmaceutical Co., Ltd.Genentech, Inc.Bristol Myers Squibb Co.Novo Nordisk A/SAmgen, Inc.Commonwealth Scientific & Industrial Research OrganisationRegeneron Pharmaceuticals, Inc.Chugai Pharmaceutical Co., Ltd.Les Laboratoires Servier SASVertex Pharmaceuticals, Inc.California Institute of TechnologyGilead Sciences, Inc.Yeda Research & Development Co. Ltd.Kyoto UniversityDuke UniversityYissum Research Development Co. Ltd.Taisho Pharmaceutical Co., Ltd.The Brigham & Women's Hospital, Inc.Millennium Pharmaceuticals, Inc.University of British ColumbiaFourth Military Medical UniversityFourth Military Medical UniversityC.H. Boehringer Sohn AG & Co. KGHuman Genome Sciences, Inc.UCB SAImmatics Biotechnologies GmbHTaiho Pharmaceutical Co., Ltd.Yakult Honsha Co., Ltd.Array BioPharma, Inc.
Janssen Pharmaceutica NVALZA Corp.Genzyme Corp.SyntheX, Inc.ZymoGenetics, Inc.Immatics Biotechnologies GmbHArray BioPharma, Inc.Alnylam Pharmaceuticals, Inc.ImmunoGen, Inc.Cephalon, Inc.Xcellerex, Inc.Seagen Inc.Rigel Pharmaceuticals, Inc.Sangamo Therapeutics, Inc.Sunovion Pharmaceuticals, Inc.Biogen, Inc.Immunomedics, Inc.Medarex, Inc.PTC Therapeutics, Inc.Xencor, Inc.CuraGen Corp.Juno Therapeutics, Inc.Amicus Therapeutics, Inc.SAGE Therapeutics, Inc.AiCuris GmbH & Co. KGSarepta Therapeutics, Inc.AC Immune SAInterMune, Inc.Precigen, Inc.LifeCell Corp.
PTC Therapeutics, Inc.Sarepta Therapeutics, Inc.Italfarmaco SpANobelpharma Co., Ltd.ReveraGen BioPharma, Inc.Adienne SASolid Biosciences, Inc.Epirium Bio, Inc.Summit Therapeutics Ltd.
Genentech, Inc.Janssen Pharmaceutica NVMonsanto Co.Massachusetts Institute of TechnologyBoehringer Ingelheim Pharmaceuticals, Inc.CJ CheilJedang Corp.Regeneron Pharmaceuticals, Inc.The Johns Hopkins UniversityChugai Pharmaceutical Co., Ltd.Les Laboratoires Servier SASShionogi & Co., Ltd.Research Institute of Industrial Science & TechnologyYeda Research & Development Co. Ltd.Kansai Paint Co., Ltd.Sichuan Agricultural UniversityAutoliv Development ABGrünenthal GmbHJEOL Ltd.Sumitomo Pharma Co., Ltd.Dana-Farber Cancer Institute, Inc.Incyte Corp.Yissum Research Development Co. Ltd.Ionis Pharmaceuticals, Inc.University of MinnesotaPurdue Research FoundationLife Technologies Corp.Syngenta Ltd.Taisho Pharmaceutical Co., Ltd.Biogen MA, Inc.The Brigham & Women's Hospital, Inc.
Solid Biosciences, Inc.Rocket Pharmaceuticals Ltd.
Genentech, Inc.Janssen Pharmaceutica NVCJ CheilJedang Corp.Japan Tobacco, Inc.The Johns Hopkins UniversityChugai Pharmaceutical Co., Ltd.Les Laboratoires Servier SASMitsubishi Tanabe Pharma Corp.Shionogi & Co., Ltd.Yeda Research & Development Co. Ltd.Grünenthal GmbHSumitomo Pharma Co., Ltd.Dana-Farber Cancer Institute, Inc.Yissum Research Development Co. Ltd.Ionis Pharmaceuticals, Inc.Purdue Research FoundationTaisho Pharmaceutical Co., Ltd.The Brigham & Women's Hospital, Inc.Yale UniversityNational University of SingaporeMeiji Seika Pharma Co., Ltd.Agency for Science, Technology & ResearchOno Pharmaceutical Co., Ltd.CHIESI Farmaceutici SpANational Research Council of CanadaEmory UniversityNew York UniversityWashington University in St. LouisImmatics Biotechnologies GmbHTaiho Pharmaceutical Co., Ltd.