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Sanofi A/SGenzyme Corp.SyntheX, Inc.Biogen, Inc.NPS PHARMS INCSarepta Therapeutics, Inc.Zambon SpATranslate Bio, Inc.Newron Pharmaceuticals SpAGénéthonInsmed, Inc.bluebird bio, Inc.Arvinas Operations, Inc.Shire Canada, Inc.Arcturus Therapeutics, Inc.Synageva BioPharma Corp.Synlogic Operating Co., Inc.Mitobridge, Inc.Transkaryotic Therapies, Inc.Vicore Pharma ABSoligenix, Inc.Eiger BioPharmaceuticals, Inc.TWi Biotechnology, Inc.AI TherapeuticsRecordati SpAHomology Medicines, Inc.Applied Genetic Technologies Corp.Healx Ltd.Stridebio, Inc.Arvinas, Inc.
F. Hoffmann-La Roche Ltd.Takeda Pharmaceutical Co., Ltd.Bayer HealthCare Pharmaceuticals, Inc.Bristol Myers Squibb Co.Sanofi A/SNovo Nordisk A/SAmgen, Inc.Baxter International, Inc.Nippon Kayaku Co., Ltd.CJ CheilJedang Corp.Japan Tobacco, Inc.Regeneron Pharmaceuticals, Inc.Chugai Pharmaceutical Co., Ltd.Les Laboratoires Servier SASShionogi & Co., Ltd.Gilead Sciences, Inc.Yeda Research & Development Co. Ltd.Grünenthal GmbHSumitomo Pharma Co., Ltd.Ionis Pharmaceuticals, Inc.Ono Pharmaceutical Co., Ltd.Celgene Corp.CHIESI Farmaceutici SpASigma-Tau Industrie Farmaceutiche Riunite SpATachi-S Co., Ltd.New York UniversityUCB SABTG Ltd.ZymoGenetics, Inc.Technion Research & Development Foundation Ltd.